Enzyme replacement therapy for late-onset Pompe disease

To assess the effects of ERT in people with LOPD.

This is a protocol.

Health topics:

Child health > Genetic disorders > Inborn errors of metabolism

Child health > Neurology > Neuromuscular disease: general treatments

Neurology > Neuromuscular disease: general treatments

Published:

20 April 2018

Authors:

Sharma R, Hughes D, Ramaswami U, Cole D, Roberts M, Hendriksz CJ, Stepien KM, Krishan A, Jahnke N

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Citation
Sharma R, Hughes D, Ramaswami U, Cole D, Roberts M, Hendriksz CJ, Stepien KM, Krishan A, Jahnke N. Enzyme replacement therapy for late-onset Pompe disease. Cochrane Database of Systematic Reviews 2018, Issue 4. Art. No.: CD012993. DOI: 10.1002/14651858.CD012993